Sarepta Announces Positive Topline Three-Year EMBARK Results Showing ELEVIDYS Significantly Slows Disease Progression on Key Functional Measures in Ambulatory Duchenne Patients

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Sarepta Announces Positive Topline Three-Year Embark Results Showing Elevidys Significantly Slows Disease Progression On Key Functional Measures In Ambulatory Duchenne Patients

By Sarepta Therapeutics

At a mean age of 9 years old, ELEVIDYS-treated patients achieved mean North Star Ambulatory Assessment (NSAA) scores above baseline three years after treatment (n=52) ELEVIDYS gene therapy demonstrated 70% or greater reduction in the rate of decline ...Read more