FDA must catch up to genetic therapies for young children like baby KJ

Science

Fda Must Catch Up To Genetic Therapies For Young Children Like Baby Kj

By statnews.com

In 2018, my daughter, Mila, became the first person in the world to receive a medicine designed for one person, an antisense oligonucleotide (ASO) called “milasen.” Last week, the world received the breaking news that a baby named KJ had received the ...Read more