
Science
Fda Must Catch Up To Genetic Therapies For Young Children Like Baby Kj
By statnews.com
In 2018, my daughter, Mila, became the first person in the world to receive a medicine designed for one person, an antisense oligonucleotide (ASO) called “milasen.”
Last week, the world received the breaking news that a baby named KJ had received the ...Read more